1 Report Overview
1.1 Objectives of the Study
1.2 Introduction to Rare Diseases Market
1.3 What This Report Delivers
1.4 Why You Should Read This Report
1.5 Key Questions Answered by This Analytical Report Include:
1.6 Who is This Report For?
1.7 Methodology
1.7.1 Market Definitions
1.7.2 Market Evaluation & Forecasting Methodology
1.7.3 Data Validation
1.7.3.1 Primary Research
1.7.3.2 Secondary Research
1.8 Frequently Asked Questions (FAQs)
1.9 Associated Reports
1.10 About
2 Executive Summary
3 Market Overview
3.1 Key Findings
3.2 Market Dynamics
3.2.1 Market Driving Factors
3.2.1.1 Increasing Number of Approval Driving Market Growth
3.2.1.2 Robust Pipeline by Major Players
3.2.1.2.1 Pfizer Rare Disease Pipeline
3.2.1.2.2 Sanofi Genzyme Corporation Rare Disease Pipeline
3.2.1.2.3 Novo Nordisk Rare Disease Pipeline
3.2.1.3 Increasing Awareness
3.2.2 Market Restraining Factors
3.2.2.1 High Research and Development Costs
3.2.2.2 High Entry Barriers to Challenge Market Growth
3.2.2.3 Physical Management of Patients Likely to Challenge Market Growth
3.2.3 Market Opportunities
3.2.3.1 Increasing Demand from Emerging Economies
3.2.3.2 Home-based Care Anticipated to Offer Lucrative Growth Prospects
3.2.3.3 Increasing Government Support
3.2.3.4 Rare Diseases Clinical Activity by Indication
3.3 COVID-19 Impact Analysis
3.4 Porter’s Five Forces Analysis
3.4.1 Bargaining Power of Buyers (Low)
3.4.2 Bargaining Power of Suppliers (medium)
3.4.3 Threat of Substitutes (Low)
3.4.4 Threat of New Entrants (Low)
3.4.5 Industry Rivalry (High)
4 Rare Diseases Market Analysis by Diseases
4.1 Key Findings
4.2 Diseases Segment: Market Attractiveness Index
4.3 Rare Diseases Market Size Estimation and Forecast by Diseases
4.4 Cancer
4.4.1 Market Forecast by Region, 2023-2033 (US$ bn)
4.4.2 Market Share by Region, 2023 & 2033 (%)
4.5 Metabolic Diseases
4.5.1 Market Forecast by Region, 2023-2033 (US$ bn)
4.5.2 Market Share by Region, 2023 & 2033 (%)
4.6 Neurological Conditions
4.6.1 Market Forecast by Region, 2023-2033 (US$ bn)
4.6.2 Market Share by Region, 2023 & 2033 (%)
4.7 Hematologic Disorders
4.7.1 Market Forecast by Region, 2023-2033 (US$ bn)
4.7.2 Market Share by Region, 2023 & 2033 (%)
4.8 Infectious Diseases
4.8.1 Market Forecast by Region, 2023-2033 (US$ bn)
4.8.2 Market Share by Region, 2023 & 2033 (%)
4.9 Musculoskeletal Disorders
4.9.1 Market Forecast by Region, 2023-2033 (US$ bn)
4.9.2 Market Share by Region, 2023 & 2033 (%)
4.10 Cardiovascular Disorders
4.10.1 Market Forecast by Region, 2023-2033 (US$ bn)
4.10.2 Market Share by Region, 2023 & 2033 (%)
4.11 Others
4.11.1 Market Forecast by Region, 2023-2033 (US$ bn)
4.11.2 Market Share by Region, 2023 & 2033 (%)
5 Rare Diseases Market Analysis by Type
5.1 Key Findings
5.2 Type Segment: Market Attractiveness Index
5.3 Rare Diseases Market Size Estimation and Forecast by Type
5.4 Non-biologics
5.4.1 Market Forecast by Region, 2023-2033 (US$ bn)
5.4.2 Market Share by Region, 2023 & 2033 (%)
5.5 Biologics
5.5.1 Market Forecast by Region, 2023-2033 (US$ bn)
5.5.2 Market Share by Region, 2023 & 2033 (%)
6 Rare Diseases Market Analysis by End-users
6.1 Key Findings
6.2 End-users Segment: Market Attractiveness Index
6.3 Rare Diseases Market Size Estimation and Forecast by End-users
6.4 Specialty Pharmacies
6.4.1 Market Forecast by Region, 2023-2033 (US$ bn)
6.4.2 Market Share by Region, 2023 & 2033 (%)
6.5 Hospital Pharmacies
6.5.1 Market Forecast by Region, 2023-2033 (US$ bn)
6.5.2 Market Share by Region, 2023 & 2033 (%)
6.6 Retail Pharmacies
6.6.1 Market Forecast by Region, 2023-2033 (US$ bn)
6.6.2 Market Share by Region, 2023 & 2033 (%)
7 Rare Diseases Market Analysis by Age
7.1 Key Findings
7.2 Age Segment: Market Attractiveness Index
7.3 Rare Diseases Market Size Estimation and Forecast by Age
7.4 Adult
7.4.1 Market Forecast by Region, 2023-2033 (US$ bn)
7.4.2 Market Share by Region, 2023 & 2033 (%)
7.5 Pediatric
7.5.1 Market Forecast by Region, 2023-2033 (US$ bn)
7.5.2 Market Share by Region, 2023 & 2033 (%)
8 Rare Diseases Market Analysis by Region
8.1 Key Findings
8.2 Regional Market Size Estimation and Forecast
9 North America Rare Diseases Market Analysis
9.1 Key Findings
9.2 North America Rare Diseases Market Attractiveness Index
9.3 Market Size by Country, 2023, 2028 & 2033 (US$ bn)
9.4 Market Size Estimation and Forecast by Country, 2023-2033 (US$ bn)
9.5 Market Size Estimation and Forecast by Diseases, 2023-2033 (US$ bn)
9.6 Market Size Estimation and Forecast by Type, 2023-2033 (US$ bn)
9.7 Market Size Estimation and Forecast by End-users, 2023-2033 (US$ bn)
9.8 Market Size Estimation and Forecast by Age, 2023-2033 (US$ bn)
9.9 U.S. Rare Diseases Market Analysis
9.10 Canada Rare Diseases Market Analysis
10 Europe Rare Diseases Market Analysis
10.1 Key Findings
10.2 Europe Rare Diseases Market Attractiveness Index
10.3 Market Size by Country, 2023, 2028 & 2033 (US$ bn)
10.4 Market Size Estimation and Forecast by Country, 2023-2033 (US$ bn)
10.5 Market Size Estimation and Forecast by Diseases, 2023-2033 (US$ bn)
10.6 Market Size Estimation and Forecast by Type, 2023-2033 (US$ bn)
10.7 Market Size Estimation and Forecast by End-users, 2023-2033 (US$ bn)
10.8 Market Size Estimation and Forecast by Age, 2023-2033 (US$ bn)
10.9 Germany Rare Diseases Market Analysis
10.10 UK Rare Diseases Market Analysis
10.11 France Rare Diseases Market Analysis
10.12 Italy Rare Diseases Market Analysis
10.13 Spain Rare Diseases Market Analysis
10.14 Russia Rare Diseases Market Analysis
10.15 Rest of Europe Rare Diseases Market Analysis
11 Asia Pacific Rare Diseases Market Analysis
11.1 Key Findings
11.2 Asia Pacific Rare Diseases Market Attractiveness Index
11.3 Market Size by Country, 2023, 2028 & 2033 (US$ bn)
11.4 Market Size Estimation and Forecast by Country, 2023-2033 (US$ bn)
11.5 Market Size Estimation and Forecast by Diseases, 2023-2033 (US$ bn)
11.6 Market Size Estimation and Forecast by Type, 2023-2033 (US$ bn)
11.7 Market Size Estimation and Forecast by End-users, 2023-2033 (US$ bn)
11.8 Market Size Estimation and Forecast by Age, 2023-2033 (US$ bn)
11.9 Japan Rare Diseases Market Analysis
11.10 China Rare Diseases Market Analysis
11.11 India Rare Diseases Market Analysis
11.12 Australia Rare Diseases Market Analysis
11.13 South Korea Rare Diseases Market Analysis
11.14 Rest of Asia Pacific Rare Diseases Market Analysis
12 Latin America Rare Diseases Market Analysis
12.1 Key Findings
12.2 Latin America Rare Diseases Market Attractiveness Index
12.3 Market Size by Country, 2023, 2028 & 2033 (US$ bn)
12.4 Market Size Estimation and Forecast by Country, 2023-2033 (US$ bn)
12.5 Market Size Estimation and Forecast by Diseases, 2023-2033 (US$ bn)
12.6 Market Size Estimation and Forecast by Type, 2023-2033 (US$ bn)
12.7 Market Size Estimation and Forecast by End-users, 2023-2033 (US$ bn)
12.8 Market Size Estimation and Forecast by Age, 2023-2033 (US$ bn)
12.9 Brazil Rare Diseases Market Analysis
12.10 Mexico Rare Diseases Market Analysis
12.11 Rest of Latin America Rare Diseases Market Analysis
13 MEA Rare Diseases Market Analysis
13.1 Key Findings
13.2 MEA Rare Diseases Market Attractiveness Index
13.3 Market Size by Country, 2023, 2028 & 2033 (US$ bn)
13.4 Market Size Estimation and Forecast by Country, 2023-2033 (US$ bn)
13.5 Market Size Estimation and Forecast by Diseases, 2023-2033 (US$ bn)
13.6 Market Size Estimation and Forecast by Type, 2023-2033 (US$ bn)
13.7 Market Size Estimation and Forecast by End-users, 2023-2033 (US$ bn)
13.8 Market Size Estimation and Forecast by Age, 2023-2033 (US$ bn)
13.9 GCC Rare Diseases Market Analysis
13.10 South Africa Rare Diseases Market Analysis
13.11 Rest of MEA Rare Diseases Market Analysis
14 Company Profiles
14.1 AbbVie Inc.
14.1.1 Company Snapshot
14.1.2 Company Overview
14.1.3 Financial Analysis
14.1.3.1 Net Revenue, 2015-2022
14.1.3.2 Regional Market Shares, 2021
14.1.3.3 Gross Profit, 2015-2022
14.1.3.4 R&D, 2015-2022
14.1.4 Product Benchmarking
14.2 Alexion Pharmaceuticals, Inc. (AstraZeneca)
14.2.1 Company Snapshot
14.2.2 Company Overview
14.2.3 Product Benchmarking
14.2.4 Strategic Outlook
14.3 Amgen Inc.
14.3.1 Company Snapshot
14.3.2 Company Overview
14.3.3 Financial Analysis
14.3.3.1 Net Revenue, 2015-2022
14.3.3.2 Regional Market Shares, 2022
14.3.3.3 Gross Profit, 2015-2022
14.3.3.4 R&D, 2015-2022
14.3.4 Product Benchmarking
14.3.5 Strategic Outlook
14.4 Biogen Inc.
14.4.1 Company Snapshot
14.4.2 Company Overview
14.4.3 Financial Analysis
14.4.3.1 Net Revenue, 2015-2021
14.4.3.2 Gross Profit, 2015-2021
14.4.3.3 R&D, 2015-2021
14.4.4 Product Benchmarking
14.4.5 Strategic Outlook
14.5 F. Hoffmann-La Roche Ltd.
14.5.1 Company Snapshot
14.5.2 Company Overview
14.5.3 Financial Analysis
14.5.3.1 Net Revenue, 2015-2021
14.5.3.2 Gross Profit, 2015-2021
14.5.3.3 R&D, 2015-2021
14.5.4 Product Benchmarking
14.5.5 Strategic Outlook
14.6 Johnson & Johnson Services, Inc.
14.6.1 Company Snapshot
14.6.2 Company Overview
14.6.3 Financial Analysis
14.6.3.1 Net Revenue, 2015-2022
14.6.3.2 Regional Market Shares, 2021
14.6.3.3 Gross Profit, 2015-2022
14.6.3.4 R&D, 2015-2022
14.6.4 Product Benchmarking
14.6.5 Strategic Outlook
14.7 Merck & Co Inc.
14.7.1 Company Snapshot
14.7.2 Company Overview
14.7.3 Financial Analysis
14.7.3.1 Net Revenue, 2015-2022
14.7.3.2 Regional Market Shares, 2021
14.7.3.3 Gross Profit, 2015-2022
14.7.3.4 R&D, 2015-2022
14.7.4 Product Benchmarking
14.8 Novartis AG
14.8.1 Company Snapshot
14.8.2 Company Overview
14.8.3 Financial Analysis
14.8.3.1 Net Revenue, 2015-2022
14.8.3.2 Regional Market Shares, 2021
14.8.3.3 Gross Profit, 2015-2022
14.8.3.4 R&D, 2015-2022
14.8.4 Product Benchmarking
14.8.5 Strategic Outlook
14.9 Pfizer Inc.
14.9.1 Company Snapshot
14.9.2 Company Overview
14.9.3 Financial Analysis
14.9.3.1 Net Revenue, 2015-2022
14.9.3.2 Regional Market Shares, 2021
14.9.3.3 Gross Profit, 2015-2022
14.9.3.4 R&D, 2015-2022
14.9.4 Product Benchmarking
14.9.5 Strategic Outlook
14.10 Sanofi S.A.
14.10.1 Company Snapshot
14.10.2 Company Overview
14.10.3 Financial Analysis
14.10.3.1 Net Revenue, 2015-2022
14.10.3.2 Regional Market Shares, 2021
14.10.3.3 Gross Profit, 2015-2022
14.10.3.4 R&D, 2015-2022
14.10.4 Product Benchmarking
14.11 Takeda Pharmaceuticals
14.11.1 Company Snapshot
14.11.2 Company Overview
14.11.3 Financial Analysis
14.11.3.1 Net Revenue, 2015-2022
14.11.3.2 Gross Profit, 2015-2022
14.11.3.3 R&D, 2015-2022
14.11.4 Product Benchmarking
14.11.5 Strategic Outlook
14.12 Teva Pharmaceuticals
14.12.1 Company Snapshot
14.12.2 Company Overview
14.12.3 Financial Analysis
14.12.3.1 Net Revenue, 2015-2021
14.12.3.2 Regional Market Shares, 2021
14.12.3.3 Gross Profit, 2015-2021
14.12.3.4 R&D, 2015-2021
14.12.4 Product Benchmarking
14.12.5 Strategic Outlook
14.13 Bristol-Myers Squibb Company
14.13.1 Company Snapshot
14.13.2 Company Overview
14.13.3 Financial Analysis
14.13.3.1 Net Revenue, 2015-2022
14.13.3.2 Gross Profit, 2015-2022
14.13.3.3 R&D, 2015-2022
14.13.4 Product Benchmarking
14.13.5 Strategic Outlook
15 Conclusion and Recommendations
15.1 Concluding Remarks
15.2 Recommendations for Market Players